Title : Therapeutic efficacy of rscAAVrh74.miniCMV.LIPA gene therapy in a mouse model of lysosomal acid lipase deficiency - Lam_2022_Mol.Ther.Methods.Clin.Dev_26_413 |
Author(s) : Lam P , Ashbrook A , Zygmunt DA , Yan C , Du H , Martin PT |
Ref : Mol Ther Methods Clin Dev , 26 :413 , 2022 |
Abstract : Lam_2022_Mol.Ther.Methods.Clin.Dev_26_413 |
ESTHER : Lam_2022_Mol.Ther.Methods.Clin.Dev_26_413 |
PubMedSearch : Lam_2022_Mol.Ther.Methods.Clin.Dev_26_413 |
PubMedID: 36092360 |
Gene_locus related to this paper: mouse-1llip , human-LIPA |
Gene_locus related to this paper: mouse-1llip , human-LIPA |
Lam P, Ashbrook A, Zygmunt DA, Yan C, Du H, Martin PT (2022)
Therapeutic efficacy of rscAAVrh74.miniCMV.LIPA gene therapy in a mouse model of lysosomal acid lipase deficiency
Mol Ther Methods Clin Dev
26 :413
Lam P, Ashbrook A, Zygmunt DA, Yan C, Du H, Martin PT (2022)
Mol Ther Methods Clin Dev
26 :413